A retrospective, single-center study out of the Czech Republic tested the safety and efficacy of unilateral interlaminar fenestration (UILF) on the convex side in cases of SMA that also exhibit severe ...
Intrathecal drug delivery involves administering analgesic medications directly into the cerebrospinal fluid, thereby achieving targeted pain relief while minimising systemic side effects. This method ...
Onasemnogene abeparvovec-brve is the first gene replacement therapy approved for SMA patients aged 2 years and older, expanding access beyond infants. Phase 3 trials demonstrated significant motor ...
Some results have been hidden because they may be inaccessible to you
Show inaccessible results